Lifesaving gene therapy for kids is world’s priciest drug at $4.25M

Enlarge / A mom along with her twin 6-year-old boys who’ve metachromatic leukodystrophy, a genetic illness that leaves them unable to maneuver. Picture taken on September 3, 2004. In a medical triumph, US Meals and Drug Administration on Monday approved a gene therapy that seems to trounce a uncommon, tragic illness that progressively steals kids’s … Read more